AVROBIO’s optimized lentiviral vectors demonstrate significant glycogen reduction in the muscle and central nervous system of Pompe disease mouse model Investigational New Drug (IND)-enabling proof-of ...
La version audio de cet article est générée par la synthèse vocale, une technologie basée sur l’intelligence artificielle. Le gouvernement de l’Île-du-Prince-Édouard élargit l’accès au Programme de ...
“Funding initiatives like Amicus Ignite can play a vital role in driving meaningful improvements for people living with rare diseases such as Pompe disease. The calibre and creativity of the ...
CAMBRIDGE, Mass.--(BUSINESS WIRE)--AVROBIO, Inc. (Nasdaq: AVRO), a leading clinical-stage gene therapy company with a mission to free people from a lifetime of genetic disease, today announced new ...